Ryan Flinn

Researchers have suggested that uniform evidence standards and reporting requirements could help speed patient access to cell and gene therapies and help ensure consistent safety and efficacy evaluations.

Solid Biosciences’ gene therapy uses a shortened version of the dystrophin protein, which is engineered to mimic the key functions of full-length dystrophin and allows it be delivered more effectively to muscle cells.

Risk factors for secondary skin cancer after blood or marrow transplant include those who had treatment with a monoclonal antibody, chronic graft-versus-host disease and posttransplant immunosuppression.

A mouse study at Memorial Sloan Kettering Cancer Center has found that adding Nef, a protein from HIV, allows donor CAR T cells to avoid detection by the immune system while still attacking tumors.

A novel AI model was able to achieve 99.86% accuracy for diagnosing skin conditions, even in people with darker skin tones or excessive hair.

Becky Kamowitz was appointed executive director of The Skin Cancer Foundation in January 2025. She talks about the organization’s priorities for the coming year.

President Trump signed an executive order on the day of his inauguration that created doubts about the future of a program that helps state Medicaid programs pay for expensive cell and gene therapy.

In a review of previous studies, researchers found that the images seen on social media contribute to taking actions that are both beneficial with patients seeking dermatological care and unfavorable with increased exposure to UV radiation for a better tan.

A small study of 18 patients with skin cancer found that the combination of vitamin D and chemotherapy provided an immune response that lasted up to five years.

Few studies in this analysis assessed the accuracy of AI in detecting melanoma in diverse skin tones.

Some muscles are resistant to the loss of motor neurons seen in patients with spinal muscular atrophy, and new research has discovered that even in muscles that appeared resistant to SMA, subtle changes had occurred at the cellular level.

The combination of Spinraza and Zolgensma could improve clinical outcomes in infants with spinal muscular atrophy without added risks.

A new study finds that that eczema can worsen when air quality drops from good to moderate levels on the Environmental Protection Agency’s Air Quality Index.

Preserving the ability to swallow reduces the need for invasive interventions and lowers the risk of life-threatening complications such as aspiration pneumonia.

Researchers reviewed 900 Reddit posts to assess opinions about the increasingly popular class of drugs.

Roche’s Evrysdi is the market leader among the drugs for spinal muscular atrophy. Biogen’s Spinraza has struggled, but company officials express confidence about future sales.

In a meta-analysis of 57 studies, Zolgensma achieved a 95% survival rate and reduced the number of patients requiring ventilatory support.

The campaign for hand eczema is the latest in a number of high-cost campaigns to raise awareness of dermatological conditions.

Repigmentation case is just the third that has been reported.

The study drew on data from the RESTORE registry for 34 patients with tracheostomies who received Zolgensma (onasemnogene abeparvovec).

Roche’s Evrysdi (risdiplam) is the market leader among the drugs for spinal muscular atrophy (SMA). Biogen’s Spinraza (nusinersen) has struggled, but company officials express confidence about future sales.

Ebglyss also provided meaningful improvements in difficult-to-treat face and hand dermatitis.

In a response to a survey, caregivers of people with spinal muscular atrophy identified the risk of severe adverse events and the need for permanent ventilation as the most important factors in treatment decisions. Access to treatment, including cost and availability, ranked third.

Some prior research had shown that gene therapy would not lower the amount of time children spend on ventilator support.

Research shows that after 60 months of treatment, 38% of patients achieved complete remission.

Two years after treatment, both girls show normal motor function and no signs of spinal muscular atrophy symptoms.

Mental health and vitiligo treatment outcomes may be associated because of a brain-skin axis, a pathway that links emotional stress to skin conditions.

Apitegromab works by targeting a protein called myostatin that limits muscle growth and is designed to be used alongside existing spinal muscular atrophy (SMA) treatments.

Previous research has shown an association between atopic dermatitis and obesity. But these findings elaborate on that observation and point to a connection to abnormal lipid metabolism and elevated "bad" LDL cholesterol levels.